Intramuscular Administration of AAV1-Lipoprotein Lipase(S447X) Lowers Triglycerides in Lipoprotein Lipase-Deficient Patients

Erik S. Stroes, Melchior C. Nierman, Janneke J. Meulenberg, Remco Franssen, Jaap Twisk, C. Pieter Henny, Mario M. Maas, Aeilko H. Zwinderman, Colin Ross, Eleonora Aronica, Katherine A. High, Marcel M. Levi, Michael R. Hayden, John J. Kastelein, Jan Albert Kuivenhoven

Research output: Contribution to journalArticleAcademicpeer-review

189 Citations (Scopus)
Original languageEnglish
Pages (from-to)2303-U264
JournalArteriosclerosis, Thrombosis, and Vascular Biology
Volume28
Issue number12
DOIs
Publication statusPublished - 2008

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