Thirty years beyond discovery-Clinical trials in succinic semialdehyde dehydrogenase deficiency, a disorder of GABA metabolism

K.R. Vogel, P.L. Pearl, W.H. Theodore, R.C. McCarter, C.A.J.M. Jakobs, K.M. Gibson

Research output: Contribution to journalArticleAcademicpeer-review

47 Citations (Scopus)
Original languageEnglish
Pages (from-to)401-410
JournalJournal of Inherited Metabolic Disease
Volume36
Issue number3
DOIs
Publication statusPublished - 2013

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