Research output per year
Research output per year
Research output
- 4 Article
Search results
-
2024
In vivo base editing of a pathogenic Eif2b5 variant improves vanishing white matter phenotypes in mice
Böck, D., Revers, I. M., Bomhof, A. S. J., Hillen, A. E. J., Boeijink, C., Kissling, L., Egli, S., Moreno-Mateos, M. A., van der Knaap, M. S., van Til, N. P. & Schwank, G., 1 May 2024, In: Molecular therapy. 32, 5, p. 1328-1343 16 p.Research output: Contribution to journal › Article › Academic › peer-review
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2023
Focal lesions following intracerebral gene therapy for mucopolysaccharidosis IIIA
Bugiani, M., Abbink, T. E. M., Edridge, A. W. D., van der Hoek, L., Hillen, A. E. J., van Til, N. P., Hu-A-Ng, G. V., Breur, M., Aiach, K., Drevot, P., Hocquemiller, M., Laufer, R., Wijburg, F. A. & van der Knaap, M. S., Jun 2023, In: Annals of clinical and translational neurology. 10, 6, p. 904-917 14 p.Research output: Contribution to journal › Article › Academic › peer-review
Open Access2 Citations (Scopus) -
2021
Efficient lentiviral transduction method to gene modify cord blood CD8(+) T cells for cancer therapy applications
Lo Presti, V., Cornel, A. M., Plantinga, M., Dunnebach, E., Kuball, J., Boelens, J. J., Nierkens, S. & van Til, N. P., 11 Jun 2021, In: Molecular Therapy - Methods and Clinical Development. 21, p. 357-368 12 p.Research output: Contribution to journal › Article › Academic › peer-review
Open Access8 Citations (Scopus) -
2014
Angiopoietin-like protein 3 promotes preservation of stemness during ex vivo expansion of murine hematopoietic stem cells
Farahbakhshian, E., Verstegen, M. M., Visser, T. P., Kheradmandkia, S., Geerts, D., Arshad, S., Riaz, N., Grosveld, F., van Til, N. P. & Meijerink, J. P. P., 2014, In: PLOS ONE. 9, 8, p. e105642Research output: Contribution to journal › Article › Academic › peer-review