Rare diseases and effective treatments: are we delivering?

Lucio Luzzatto, Carla E. M. Hollak, Timothy M. Cox, Arrigo Schieppati, Christoph Licht, Helena Kääriäinen, Giampaolo Merlini, Franz Schaefer, Steven Simoens, Luca Pani, Silvio Garattini, Giuseppe Remuzzi

Research output: Contribution to journalEditorialAcademicpeer-review

47 Citations (Scopus)
Original languageEnglish
Pages (from-to)750-752
JournalLancet
Volume385
Issue number9970
DOIs
Publication statusPublished - 2015

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