Study protocol, rationale and recruitment in a European multi-centre randomized controlled trial to determine the efficacy and safety of azithromycin maintenance therapy for 6 months in primary ciliary dyskinesia

Helene E. Kobbernagel, Frederik F. Buchvald, Eric G. Haarman, Carmen Casaulta, Samuel A. Collins, Claire Hogg, Claudia E. Kuehni, Jane S. Lucas, Heymut Omran, Alexandra L. Quittner, Claudius Werner, Kim G. Nielsen

Research output: Contribution to journalArticleAcademicpeer-review

49 Citations (Scopus)
Original languageEnglish
Article number104
JournalBMC Pulmonary Medicine
Volume16
DOIs
Publication statusPublished - 22 Jul 2016

Keywords

  • Azithromycin
  • Exacerbation
  • Health-related quality of life
  • Lung clearance index
  • Multiple breath washout
  • Primary ciliary dyskinesia
  • QOL-PCD

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